StemCell Therapy

Gene therapy delivers DNA into a patients cells to replace faulty or missing genes or adds new genes in an attempt to cure diseases or to make changes so the body is better able to fight off disease. The DNA for a gene or genes is carried into a patients cells by a delivery vehicle called a vector, typically a specially engineered virus. The vector then inserts the gene(s) into the cells' DNA.

Although gene therapy is relatively new and often still considered experimental, it can provide a cure for life-threatening diseases that dont respond well to other therapies (including immunodeficiencies, metabolic disorders, and relapsed cancers) and for acute conditions that currently rely on complex and expensive life-long medication and management (such as sickle cell disease and hemophilia).

Our Gene Therapy Clinical Trials

Learn more about our gene therapy clinical trials

Dana-Farber/Boston Childrens has one the most extensive and long-running pediatric gene therapy programs in the world. Since 2010, we have treated 25 patients from 11 countries through eight gene therapy clinical trials.

Why choose Dana-Farber/Boston Childrens:

Learn more

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Gene Therapy for Pediatric Diseases | DNA Therapy - Dana ...

This entry was posted on January 13, 2017 at 1:42 am and is filed under Gene therapy. You can follow any responses to this entry through the RSS 2.0 feed. Both comments and pings are currently closed. |